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Discover Our New Heritable Thoracic Aortic Diseases E-Learning Course |
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Reflecting on VASCERN Days 2023: Two days of collaboration & knowledge exchange |
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MOOC From Lab to Clinic: Translational Research for Rare Diseases |
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The Rare disease community unites in an open letter for continued support of European Reference Networks |
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Apply for the 1st Edition of the VASCERN Summer School on Rare Vascular Diseases! |
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VASCERN Spotlights: Eva Collado González |
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Together4RD’s Position Statement on collaboration between ERNs and industry |
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Vascular Anomalies Working Group (VASCA-WG) CPMS Case Discussion |
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Patient-Centered HTAD Quality Measures Now Online! |
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2 November 2023 |
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VASCERN MSA-WG Monthly Meeting |
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7 November 2023 |
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VASCERN NEUROVASC-WG Monthly Meeting |
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14 November 2023 |
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VASCERN ePAG Monthly Meeting |
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15 November 2023 |
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VASCERN VASCA-WG Monthly Meeting |
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20 November 2023 |
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VASCERN PPL-WG Monthly Meeting |
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Establishing novel approaches to improve clinical trials for rare and ultra-rare diseases |
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A new two-stage call for proposals titled “Establishing novel approaches to improve clinical trials for rare and ultra-rare diseases” was released on July 27, 2023, under the Horizon Europe Framework Programme (HORIZON).
This project’s primary goal is to drive innovation and streamline the drug development process for rare diseases characterized by significant unmet medical needs.
The application deadline for this opportunity is November 8, 2023, at 17:00 local Brussels time. |
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A case report of sirolimus use in early fetal management of lymphatic malformation |
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Sirolimus, by targeting the mammalian target of rapamycin (mTOR) pathway, has demonstrated efficacy on lymphatic malformations (LMs) in adults and neonates. The current hypothesis is that the earlier the lesion is treated, the better it responds. This has prompted the idea that sirolimus administration might be efficacious to treat fetal LMs as well. |
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